Search Result "Duchenne muscular dystrophy (DMD)"


Developing Effective Therapy for Duchenne Muscular Dystrophy (DMD): Challenges and Promises

Journal: Current Chemical Biology
Volume: 8 Issue: 3 Year: 2014 Page: 117-131
Author(s): Trinath Ghosh,Ujjal Ghosh,Gargi Ghosh,Dabasish Malik,Shankhamala Bose,Utpal Basu

Review Article

Therapeutic Applications of CRISPR/Cas for Duchenne Muscular Dystrophy

Journal: Current Gene Therapy
Volume: 17 Issue: 4 Year: 2017 Page: 301-308
Author(s): Tatianna Wai Ying Wong,Ronald D. Cohn

Cardiovascular Surveillance of Duchenne and Becker Muscular Dystrophy and Female Carriers

Journal: Current Pediatric Reviews
Volume: 4 Issue: 3 Year: 2008 Page: 159-163
Author(s): Virginia Spehrs-Ciaffi, Pierre-Yves Jeannet, Nicole Sekarski

Antisense Oligonucleotide-Mediated Exon Skipping for Duchenne Muscular Dystrophy: Progress and Challenges

Journal: Current Gene Therapy
Volume: 12 Issue: 3 Year: 2012 Page: 152-160
Author(s): Virginia Arechavala-Gomeza,Karen Anthony,Jennifer Morgan,Francesco Muntoni

Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD)

Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 395-415
Author(s): Klaudia Kawecka,Michael Theodoulides,Yalin Hasoglu,Susan Jarmin,Hanna Kymalainen,Anita Le-Heron,Linda Popplewell,Alberto Malerba,George Dickson,Takis Athanasopoulos

Case Report open access plus

Duchenne Muscular Dystrophy Management and Treatment Access Challenges:Case Report

Journal: New Emirates Medical Journal
Volume: 4 Issue: 1 Year: 2023 Page: 1-5
Author(s): Tarek I. El-Azzabi

Pathways Disturbed in Duchenne Muscular Dystrophy

Ebook: Young People’s Visions of the World

Volume: 1 Year: 2010
Author(s): Maria A. Shkrob,Mikhail A. Pyatnitskiy,Pavel K. Golovatenko-Abramov,Ekaterina A. Kotelnikova
Doi: 10.2174/97816080543741120101

The Role of Stem Cells in Muscular Dystrophies

Journal: Current Gene Therapy
Volume: 12 Issue: 3 Year: 2012 Page: 192-205
Author(s): Mirella Meregalli,Andrea Farini,Federica Colleoni,Letizia Cassinelli,Yvan Torrente

Comparative Genomics of X-linked Muscular Dystrophies: The Golden Retriever Model

Journal: Current Genomics
Volume: 14 Issue: 5 Year: 2013 Page: 330-342
Author(s): Candice Brinkmeyer-Langford,Joe N. Kornegay

Splice Modification to Restore Functional Dystrophin Synthesis in Duchenne Muscular Dystrophy

Journal: Current Pharmaceutical Design
Volume: 16 Issue: 8 Year: 2010 Page: 988-1001
Author(s): Steve. D. Wilton, Susan Fletcher

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